New company to use CRISPR/Cas9 to correct 80% of 3000 mutations involved in Duchenne muscular dystrophy

I’m not entirely sure, but it sounded like the mutations are all on the gene that encodes for the protein dystrophin.

You are right. Change the gene via crispr, fix the problem.

The article said DMD was particularly suited to this kind of editing. But that doesn’t mean that similar technologies can’t be developed for broader use eventually.

2 Likes

Thank you for posting twinklestars! Go Crispr!

1 Like